Spotlight Session: Commercializing Gene Therapies for Hemophilia
SPOTLIGHT SESSION: COMMERCIALIZING GENE THERAPIES FOR HEMOPHILIA Compared to traditional methods for managing hemophilia, gene therapy ...
Alliance for Regenerative Medicine
CDC Webinar: New Opportunities and Challenges in Hemophilia Care
The landscape of hemophilia care is experiencing significant changes that will impact patient treatment in the coming years. We are entering a period of ...
Hemophilia Federation of America
Hemophilia A: personal perspective (Lithuanian version)
Michael, a young adult from the Netherlands, shares his perspective on living with haemophilia A. Haemophilia is rare, hereditary disease. Learn more about ...
Roche
Understanding Hemophilia
Find out more about Visual Storytelling: http://www.cast-pharma.com/pharma-biotech-marketing-solutions/?ref=yt Visualizing the coagulation cascade ...
CAST PHARMA
AMT-061 Gene Transfer in Adults with Hemophilia B: Early Results of a Phase 2b Trial
Thierry VandenDriessche, PhD discusses "AMT-061 (AAV5-Padua hFIX variant) Gene Transfer in Adults with Hemophilia B: Early Results of a Phase 2b Trial" ...
GeneTherapy
Unveiling Hemophilia A | Episode 1: The coagulation team
How does our blood coagulate? Coagulation is the process that allows people to stop bleeding. For blood clots to form, a specific sequence of events involving ...
Roche
Haemophilia & Physiotherapy Research in East Kent Hospitals
Patients and staff explain how haemophilia & physiotherapy research in East Kent is making a difference.
East Kent Hospitals University NHS Foundation Trust
What is the Ideal Factor Trough Level?
At the WFH 2017 Global Forum in Montréal, David Page led a discussion between Alok Srivastava (India), Mark Skinner (USA), Margaret Ragni (USA), and ...
WFHcommunications
Dawn Rotellini: Changes in Hemophilia
Dawn Rotellini, chief operating officer of the National Hemophilia Foundation, discusses the impact recent advances in technology and changes in policy ...
HCPLive
Bioengineered Molecules for the Management of Hemophilia: Promise and Remaining Challenges
For select webcasts and other resources from the WFH 2018 World Congress go to: http://eLearning.wfh.org/WFHCongress. In the Thursday morning session ...
WFHcommunications
The WFH Hemophilia Twinning Program: Building Relationships, Helping Improve Patient Care
The World Federation of Hemophilia (WFH) Twinning Program pairs hemophilia treatment centers and patient organizations in emerging and established ...
Pfizer
Management of Hemophilia in the Emergency Department: A Case-Based Discussion
This CME Outfitters LLC Snack features case-based learning designed to facilitate problem-solving and therefore bridge the gap between evidence and ...
CME Outfitters
Anders' Story | Raising a Child With Hemophilia
Anders' son has hemophilia. A hereditary, congenital and lifelong bleeding disorder. Hear Anders' story and his advice to others living with hemophilia. You can ...
Roche
Hemophilia B
My Antibiotics course: https://www.medicosisperfectionalis.com/products/courses/antibiotics/ SORRY, I made a MISTAKE...I said that Turner Syndrome is 43+XO.
Medicosis Perfectionalis
uniQure
Jon Garen, Chief Business Officer Lexington, MA (NASDAQ: QURE) uniQure is delivering on the promise of gene therapy, single treatments with potentially ...
Alliance for Regenerative Medicine
Moving Towards Commercialization of a Potentially Curative Gene Therapy
Moving Towards Commercialization of a Potentially Curative Gene Therapy - Chuck Bucklar Scientific Symposium from the American Society of Gene & Cell ...
ASGCT
One Year Follow-up of Patients with Hemophilia B Following SPK-9001 Gene Transfer
Thierry VandenDriessche, PhD discusses "One Year Follow-up of Patients with Hemophilia B Following SPK-9001 Gene Transfer: Health-related Quality of Life ...
GeneTherapy
Help Hemophilia of Georgia fund research for a cure
Families affected by hemophilia are anxiously waiting to find out if current gene therapy research will result in a cure. In this video, two fathers share what a cure ...
Hemophilia of Georgia
uniQure
Jon Garen, Chief Business Officer Lexington, MA (NASDAQ: QURE) uniQure is delivering on the promise of gene therapy single treatments with potentially ...
Alliance for Regenerative Medicine
About the Series | CHALLENGE ACCEPTED: Living with Hemophilia A
Watch Justin Willman explain why CHALLENGE ACCEPTED was created. We are taking the next step, overcoming barriers, and letting go of excuses when it ...
CHALLENGE ACCEPTED Show
Spark Therapeutics - OIS@AAO 2015
Spark was founded about 2 years ago with the vision of building a fully integrated gene therapy company with research and development, manufacturing, and ...
OIS: Ophthalmology Innovation & Investment
Robotic Resection of Castleman Disease in a Patient with Hemophilia A
This video won 3rd place in the 2015 Resident Video Competition! View full article here: http://www.ctsnet.org/article/robotic...
CTSNetVideo
Unveiling Hemophilia A | Episode 2: Introducing Inhibitors.
Introducing the inhibitors! In the first episode of Unveiling Hemophilia, we explained that people with type A of the disease can receive a replacement treatment ...
Roche
New England CEPAC: Hemophilia March 29, 2018 (Policy Roundtable)
Institute for Clinical and Economic Review ICER
Transforming the Lives of Children With Hemophilia: Meet Dr. Amy Dunn
Connect with a specialist: http://bit.ly/2qnVf85 Hematology care at Nationwide Children's: http://bit.ly/2eQiFQ4 Learn more about Hemophilia: http://bit.ly/2dusdwn ...
NationwideChildrens
Transforming Lives | Hemophilia A: Qaboos's story from Oman
Haemophilia A is an inherited bleeding disorder in which a person's blood doesn't clot properly. Qaboos's (a little kid from Oman) mother, shares her son's story ...
Roche
Jeff Marrazzo Discusses His Company's Hemophilia Portfolio
Jeff Marrazzo is Co-Founder and CEO of Spark Therapeutics. In this video, he discusses his company's investigational gene therapy programs focused on ...
CheckRare
Spark’s Ciulla Says Luxturna Could Be Sign of Treatment to Come
Thomas Ciulla, MD, Medical Strategy Lead, Ophthalmology at Spark Therapeutics Inc., tells OIS-TV why the retina is so challenging to fix. But gene therapy ...
OIS: Ophthalmology Innovation & Investment
Are the FDA’s Gene Therapy Guidances Good for Business?
Geoff MacKay, president and CEO of Avrobio, a gene therapy company focused on lysosomal diseases talks about the FDA's guidances they have published to ...
CheckRare
Spark Therapeutics' Pipeline Overview
Ron Philip, Chief Commercial Officer of Spark Therapeutics, discusses his company's pipeline which is focused on a range of debilitating genetic diseases, ...
CheckRare
Advances in Hemophilia A Treatments
Leonard Valentino, head of hematology at Baxalta discusses recent approved treatment options for Hemophilia A and what that means for patients in the future ...
Rare Disease Report
Breaking Through with Patrick and BioMarin’s Hemophilia Patient Advocacy Lead, Rose
Growing up with a bleeding disorder can be challenging, but BioMarin wants to talk about the ways that patients can find their own comfort and creativity.
BioMarin
Raising a Child With Hemophilia | Anders Ask (Full Version)
Anders' son has hemophilia. A hereditary, congenital and lifelong bleeding disorder. Hear Anders' story and his advice to others living with hemophilia. The films ...
Roche
New Developments in Treatment for Bleeding Disorders - Novel Therapies
New panel discussion: New Developments in Treatment for Bleeding Disorders – Novel Therapies, is a cure for hemophilia around the corner? While clotting ...
WFHcommunications
Clinical Strategies for Hemophilia with Dr. Mark Reding
Mark Reding, MD,Associate Professor of Medicine in the Division of Hematology, Oncology, and Transplantation and Director, Center for Bleeding and Clotting ...
ImpactEdunet
Gene Therapy in Hemophilia: An Introduction to AAV Vector Gene Transfer
A comprehensive educational resource designed by leading experts for the global hemophilia community to help you stay abreast of the evolving science and ...
GeneTherapy
Nuwiq - Method Of Action for Hemophilia
Twisted frame is contracted to produce medical education video for hemophilia. We have created 3D elements with accurate movements to show the details.
Twisted Frame
Gene therapy series: How does a clinical trial in gene therapy for haemophilia work? with Dan Hart
Dan Hart is Honorary Consultant Haematologist at The Royal London Hospital Centre, Barts Health NHS Trust in London, United Kingdom. He is also a member ...
European Haemophilia Consortium
Hemophilia A and B, new Phase II data confirming fitusiran and RNA interference technology
PharmaStarTV
FDA’s Efforts to Advance the Development and Approval of Cellular and Gene Therapies
FEATURED TALK: FDA'S EFFORTS TO ADVANCE THE DEVELOPMENT AND APPROVAL OF CELLULAR AND GENE THERAPIES Speaker: Peter Marks, ...
Alliance for Regenerative Medicine
A. Follenzi - Cell and gene therapy for hemophilia A
Antonia Follenzi, Università degli Studi del Piemonte Orientale “A. Avogadro”, Dip. di Scienze della Salute (Dept. of Health Sciences), Novara, ITALIA speaks on ...
Icgeb
Pfizer at the Forefront of Gene Research
Find out how Pfizer scientists are at the forefront of pharmaceutical research by using tools like gene therapy to explore possible treatments for hemophilia and ...
Pfizer
